NPR

First Gene Therapy For Inherited Disease Gets FDA Approval

The Food and Drug Administration approved Luxturna, a genetically modified virus that restores by ferrying a healthy gene into the eyes of patients born with a genetic disease that impairs sight.

The Food and Drug Administration Tuesday approved the first gene therapy to treat an inherited disease.

The treatment is called Luxturna, a genetically modified virus that ferries a healthy gene into the eyes of patients born with , a rare condition that destroys cells in the retina needed for healthy vision.

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