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Eteplirsen
August 8, 2013
eteplirsen
40 Mendell
MD
8 1
(DMD)
5,000 12
DMD dystrophin
65% dystrophin
Eteplirsen Sarepta
dystrophin 51 13%
II 2011 8 eteplirsen 12 7 12
IVs 30 mg/kg
50 mg/kg
12 24 48 dystrophin
dystrophin 12 24 dystrophin
23%
P
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1
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Eteplirsen
48 dystrophin
52% 67.3
Mendell
dystrophin
dystrophin
Mendell
dystrophin
dystrophin
Mendell
Sarepta
eteplirsen DMD
P
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