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Eteplirsen

Eteplirsen

August 8, 2013

eteplirsen


40 Mendell
MD

8 1

(DMD)

5,000 12
DMD dystrophin

65% dystrophin

Eteplirsen Sarepta
dystrophin 51 13%
II 2011 8 eteplirsen 12 7 12

IVs 30 mg/kg
50 mg/kg
12 24 48 dystrophin

dystrophin 12 24 dystrophin
23%

P
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Eteplirsen

48 dystrophin
52% 67.3

Mendell
dystrophin

dystrophin
Mendell
dystrophin

dystrophin
Mendell

Sarepta
eteplirsen DMD

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