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  • Gene Therapy 2

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    Aminath Meesan
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    Gene therapy was first proposed in 1972 and involved the first approved human trial in 1990 to treat ADA-SCID. Since then, over 1,700 clinical trials have studied various gene therapy techniques. While early failures caused skepticism, successful treatments since 2006 for conditions like Leber's congenital amaurosis and other diseases have boosted optimism in gene therapy's promise. These recent successes have led to renewed interest in gene therapy and calls to continue investing in the field.

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    continuation of gene therapy 1

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    gene therapy 2.docx

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    Gene therapy was first proposed in 1972 and involved the first approved human trial in 1990 to treat ADA-SCID. Since then, over 1,700 clinical trials have studied various gene therapy techniques. While early failures caused skepticism, successful treatments since 2006 for conditions like Leber's congenital amaurosis and other diseases have boosted optimism in gene therapy's promise. These recent successes have led to renewed interest in gene therapy and calls to continue investing in the field.

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    Attribution Non-Commercial (BY-NC)
    Download as DOCX, PDF, TXT or read online from Scribd
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    2 views1 page

    Gene Therapy 2

    Uploaded by

    Aminath Meesan
    Gene therapy was first proposed in 1972 and involved the first approved human trial in 1990 to treat ADA-SCID. Since then, over 1,700 clinical trials have studied various gene therapy techniques. While early failures caused skepticism, successful treatments since 2006 for conditions like Leber's congenital amaurosis and other diseases have boosted optimism in gene therapy's promise. These recent successes have led to renewed interest in gene therapy and calls to continue investing in the field.

    Copyright:

    Attribution Non-Commercial (BY-NC)
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    of 1

    Gene therapy

    Gene therapy was first conceptualized in 1972, with the authors urging caution before commencing gene therapy studies in humans. The first FDA-approved gene therapy experiment in the United [1] States occurred in 1990, when Ashanti DeSilva was treated forADA-SCID. Since then, over 1,700 [2] clinical trials have been conducted using a number of techniques for gene therapy. Although early clinical failures led many to dismiss gene therapy as over-hyped, clinical successes since 2006 have bolstered new optimism in the promise of gene therapy. These include successful treatment of [3][4][5][6] [7] patients with the retinal disease Leber's congenital amaurosis, X-linked SCID, ADA[8] [9] [10] SCID, adrenoleukodystrophy, chronic lymphocytic leukemia (CLL), acute lymphocytic [11] [12] [13] leukemia (ALL), multiple myeloma andParkinson's disease. These recent clinical successes have led to a renewed interest in gene therapy, with several articles in scientific and popular publications calling for continued investment in the field

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