SANSON, MARLON, G.

BSELEXT 1-E
GE-117

Structu-Journal 10- Gene Therapy

Title: Structu-Journal 10: Gene Therapy
Introduction: In this Structu-Journal, we will explore the rapidly advancing field of gene therapy,
which involves the use of genetic material to treat or cure diseases. Gene therapy has the
potential to revolutionize the way we treat many genetic and acquired diseases, including cancer,
cystic fibrosis, and muscular dystrophy. In this journal, we will examine the different types of
gene therapy, the challenges of gene delivery, and the current state of the field.
Section 1: Types of Gene Therapy
In this section, we will provide an overview of the different types of gene therapy. We will
discuss the use of gene editing tools such as CRISPR/Cas9 to correct or delete faulty genes. We
will also explore the use of gene addition therapy, which involves adding a functional copy of a
gene to cells with a faulty gene. Additionally, we will discuss the use of gene silencing therapy,
which aims to reduce or eliminate the expression of a harmful gene.
Section 2: Gene Delivery
In this section, we will examine the challenges of delivering genes to target cells in the body. We
will discuss the use of viral vectors, non-viral vectors, and physical methods of gene delivery. We
will also explore the importance of developing safe and effective delivery systems to ensure that
gene therapy is both safe and effective.
Section 3: Current State of the Field
In this section, we will provide an overview of the current state of the field of gene therapy. We
will discuss the successes and failures of clinical trials and the regulatory landscape for gene
therapy. We will also explore the ethical and social implications of gene therapy, including
concerns about access and equity.
Conclusion: In this Structu-Journal, we have explored the exciting field of gene therapy and its
potential to revolutionize the way we treat many diseases. We have seen how different types of
gene therapy can be used to correct or replace faulty genes, and how gene delivery systems are a
critical component of successful gene therapy. As the field of gene therapy continues to evolve
and mature, we can expect to see many more successes in the coming years, and a better
understanding of the ethical and social implications of this powerful technology.